Browsing by Author Vlodavets, D.
Showing results 1 to 3 of 3
Issue Date | Title | Author(s) |
May-2020 | FIREFISH Part 2: Efficacy and safety of risdiplam (RG7916) in infants with Type 1 spinal muscular atrophy (SMA) | Servais, L.; Baranello, G.; Masson, R.; Mazurkiewicz-Beldzinska, M.; Rose, K.; Vlodavets, D.; Xiong, H.; Zanoteli, E.; El-Khairi, M.; Fuerst-Recktenwald, S.; Gerber, M.; Gorni, K.; Kletzl, H.; Scalco, R.; Darras, B. T. |
Oct-2020 | FIREFISH Parts 1 and 2: 12-month pooled safety and efficacy outcomes of risdiplam (RG7916) in infants with Type 1 spinal muscular atrophy (SMA) | Servais, L.; Bloespflug-Tanguy, O.; Darras, B.; Day, J.; Deconinck, N.; Klein, A.; Masson, R.; Mazurkiewicz-Beldzinska, M.; Mercuri, E.; Rose, K.; Vlodavets, D.; Xiong, H.; Zanoteli, E.; Dodman, A.; El-Khairi, M.; Gerber, M.; Gorni, K.; Kletzl, H.; Scalco, R.; Baranello, G. |
Jun-2021 | FIREFISH Parts 1 and 2: 24-Month Safety and Efficacy of Risdiplam in Type 1 SMA | Masson, R.; Boespflug-Tanguy, O.; Darras, B. T.; Day, J. W.; Deconinck, N.; Klein, A.; Mazurkiewicz-Bedziska, M.; Mercuri, E.; Rose, K.; Servais, L.; Vlodavets, D.; Xiong, H.; Zanoteli, E.; Dodman, A.; El-Khairi, M.; Gaki, E.; Gerber, M.; Gorni, K.; Kletzl, H.; Baranello, G. |